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Clinical Trials in Non-Standard Situations
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Ethics
Clinical Trials in Non-Standard Situations
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The following resources present relevant infromation on this topic:
Recommendations for the design of small population clinical trials - PMC (nih.gov)
IRDiRC Publications & Recommendations – IRDiRC
Clinical trial designs for rare diseases: Studies developed and discussed by the International Rare Cancers Initiative - European Journal of Cancer (ejcancer.com)
The patient’s view on rare disease trial design – a qualitative study | Orphanet Journal of Rare Diseases | Full Text (biomedcentral.com)
Non-Inferiority Clinical Trials | FDA
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